Firdapse
National Institutes of Health
Papers overview
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Objective: To describe treatment challenges in Dok-7 Congenital Myasthenic Syndrome (CMS) and clinical response to 3,4 DAP in two…
What is known and Objective: Orphan drugs are used to diagnose, prevent or treat a rare disease. This Commentary aims to present…
AbstractAminopyridines are members of a family of monoamino and diamino derivatives of pyridine, and their principal mechanism of…
BioMarin Europe feels that our letter on the costs of orphan drugs such as amifampridine (Firdapse) for Lambert Eaton myasthenic…
The Department of Health for England has said it has no powers to control the price of amifampridine (marketed as Firdapse…
Amifampridina; Sindrome miastenica de Lambert Eaton; Revisio sistematica; Amifampridine; Lambert Eaton Myasthenic Syndrome…