Skip to search formSkip to main contentSkip to account menu

Firdapse

National Institutes of Health

Papers overview

Semantic Scholar uses AI to extract papers important to this topic.
2018
2018
Objective: To describe treatment challenges in Dok-7 Congenital Myasthenic Syndrome (CMS) and clinical response to 3,4 DAP in two… 
2013
2013
What is known and Objective:  Orphan drugs are used to diagnose, prevent or treat a rare disease. This Commentary aims to present… 
Review
2012
Review
2012
AbstractAminopyridines are members of a family of monoamino and diamino derivatives of pyridine, and their principal mechanism of… 
2011
2011
BioMarin Europe feels that our letter on the costs of orphan drugs such as amifampridine (Firdapse) for Lambert Eaton myasthenic… 
Review
2010
Review
2010
The Department of Health for England has said it has no powers to control the price of amifampridine (marketed as Firdapse… 
Review
2010
Review
2010
Amifampridina; Sindrome miastenica de Lambert Eaton; Revisio sistematica; Amifampridine; Lambert Eaton Myasthenic Syndrome…