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ataluren
Known as:
EC-000.2051
National Institutes of Health
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Related topics
Related topics
2 relations
Broader (1)
Oxadiazoles
Narrower (1)
PTC 124
Papers overview
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2019
2019
Ataluren in DMD Version 1.0 23.11.2019 5 a4 Pages) a Proposed Extension of Ataluren Indications in Patients with Duchenne Muscular Dystrophy (DMD) Caused by Frameshift Mutations Associated with…
A. Drăgoi
2019
Corpus ID: 213223433
This paper proposes an extension of Ataluren indications (with future deserved studies) in patients with Duchenne muscular…
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2016
2016
Ataluren: Clinical Trial Results in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
U. Schara
,
C. McDonald
,
+15 authors
S.-M. Park
2016
Corpus ID: 75717412
2015
2015
Design of a Confirmatory Phase 3, Multicenter, Randomized, Double Blind, Placebo-Controlled Study (ACT DMD) of Ataluren in Patients with Nonsense Mutation Duchenne Muscular Dystrophy
R. Spiegel
,
A. Reha
,
+4 authors
C. Wiesmann
2015
Corpus ID: 53585512
Isolated ocular distribution in double seronegative myasthenia with low density receptor-related protein 4 antibodies: a case…
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2015
2015
No STOPS: Translational read-through of nonsense mutations for the treatment of hereditary retinal disorders
Kerstin Nagel-Wolfrum
2015
Corpus ID: 116713048
H retinal dystrophies are a genetically heterogeneous group of rare disorders that causes vision defects, for which currently no…
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2015
2015
Kandidat für den Galenus-Preis 2015: Ataluren gegen Duchenne-Muskeldystrophie
Urban Vogel
Orthopädie & Rheuma
2015
Corpus ID: 190873847
2014
2014
Families’ experiences with medical research for pediatric rare diseases : a qualitative ethnographic study of parents and children participating in clinical trials for Duchenne muscular dystrophy…
Christopher J. Condin
2014
Corpus ID: 75290148
The biopharmaceutical industry has recently expanded its focus on developing new cures for rare diseases. As a growing number of…
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2014
2014
Duchenne / Becker muscular dystrophy Expectations and experiences of investigators and parents involved in a clinical trial for
H. Peay
,
A. Tibben
,
Tyler Fisher
,
Ethan Brenna
,
B. Biesecker
2014
Corpus ID: 207772201
2013
2013
Ataluren-time for a 'no–nonsense' approach to haematological malignancies
J. Loudon
2013
Corpus ID: 43954632
Abstract This article outlines the novel application of Ataluren - a readthrough agent - for the management of a number of…
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2013
2013
Ataluren: Time for a ‘No-Nonsense’ Approach to Heart Diseases
J. Loudon
Cardiovascular Drugs and Therapy
2013
Corpus ID: 30881514
2010
2010
Molecule of the month. Ataluren.
Drug News and Perspectives
2010
Corpus ID: 32622622