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migalastat

National Institutes of Health

Related topics

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6 relations

Broader (1)

1-Deoxynojirimycin
1-deoxy-galactonojirimycinN-butyldeoxygalacto-nojirimycinanalogs & derivativesmigalastat hydrochloride

Narrower (1)

GR181413A

Papers overview

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Review
2019
Review
2019
Correction to: Migalastat: A Review in Fabry Disease
The article Migalastat: A Review in Fabry Disease, written by Emma H. McCafferty, Lesley J. Scott, was originally published… 
2018
2018
Pregnancy outcome after exposure to migalastat: A case study
2018
2018
SP004EFFECTS OF LONG-TERM MIGALASTAT TREATMENT ON RENAL FUNCTION BY BASELINE PROTEINURIA IN PATIENTS (PTS) WITH FABRY DISEASE
2017
2017
84Efficacy and safety of migalastat, an oral pharmacologic chaperone for Fabry disease: results from two randomized phase 3 studies, FACETS and ATTRACT
2017
2017
Effects of treatment with migalastat on the combined endpoint of kidney globotriaosylcermide accumulation and diarrhea in patients with Fabry disease: results from the phase 3 FACETS study
2017
2017
MO068EFFICACY AND SAFETY OF MIGALASTAT, AN ORAL PHARMACOLOGICAL CHAPERONE FOR FABRY DISEASE: RENAL FINDINGS FROM TWO RANDOMIZED PHASE 3 STUDIES (FACETS AND ATTRACT)
2017
2017
Migalastat in the treatment of Fabry disease
Fabryho choroba je dědičné onemocnění s multiorgánovým postižením. Specifická léčba doposud spočívala pouze v intravenózní náhrad… 
2016
2016
Fabry disease: A pharmacological chaperone on the horizon
For more than a decade, enzyme replacement therapy represented the only treatment option for patients with Fabry disease. New… 
2015
2015
Long-term efficacy and safety of migalastat compared to enzyme replacement therapy in Fabry disease: Phase 3 study results
2014
2014
Phase 3 FACETS study of migalastat HCl for Fabry disease: post hoc GLA mutation-based identification of subjects likely to show a drug effect
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