Skip to search formSkip to main contentSkip to account menu

Sapropterin dihydrochloride

National Institutes of Health

Papers overview

Semantic Scholar uses AI to extract papers important to this topic.
Review
2015
Review
2015
BACKGROUND Phenylketonuria results from a deficiency of the enzyme phenylalanine hydroxylase. Dietary restriction of… 
2012
2012
Review
2009
Highly Cited
2008
Highly Cited
2008
Phenylketonuria (PKU) is an inherited metabolic disease characterized by phenylalanine (Phe) accumulation, which can lead to… 
2008
2008
AbstractBackground and objective: Untreated phenylketonuria is characterized by neurocognitive and neuromotor impairment, which… 
Highly Cited
2007
Highly Cited
2007
SummaryThis study aimed to evaluate the response to and safety of an 8-day course of sapropterin dihydrochloride (6R…