Myozyme
National Institutes of Health
Papers overview
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OBJECTIVE
To investigate the lowering effect on lipid and safety of proprotein convertase subtilisin/kexin type 9 (PCSK9…
The alglucosidase alfa (Myozyme®) Safety Information Packet (“previous SIP”) was updated to improve readability and content…
With dabigatran and rivaroxaban, two new promising anticoagulants (NOACs) are now approved and available in most countries…
Pompe disease is an autosomal recessive inherited glycogen storage disease, usually respiratory muscles, cardiac muscle and…
Oxyrane and BioMarin have separately reported on their next-generation enzyme replacement therapies for Pompe's disease. Both…
Pompe disease is a rare autosomal recessive lysosomal storage disease caused by deficiency of acid-a-glucosidase (GAA). This…
Introduction Monoclonal antibodies (MAbs) currently comprise the fastest growing class of protein therapeutics primarily for the…