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AAVS1 gene

Known as: AAV, AAVS1, adeno-associated virus integration site 1 
National Institutes of Health

Related topics

Related topics

1 relation
Dependovirus

Papers overview

Semantic Scholar uses AI to extract papers important to this topic.
Highly Cited
2018
Highly Cited
2018
Long-term Evaluation of AAV-CRISPR Genome Editing for Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a monogenic disorder and a candidate for therapeutic genome editing. There have been several… 
Review
2018
Review
2018
Pharmaceutical Development of AAV-Based Gene Therapy Products for the Eye
A resurgence of interest and investment in the field of gene therapy, driven in large part by advances in viral vector technology… 
Review
2016
Review
2016
Adeno-associated virus (AAV) vectors in cancer gene therapy.
Highly Cited
2016
Highly Cited
2016
Organization of the connections between claustrum and cortex in the mouse
The connections between the claustrum and the cortex in mouse are systematically investigated with adeno‐associated virus (AAV… 
Review
2013
Review
2013
Humoral Immune Response to AAV
Adeno-associated virus (AAV) is a member of the family Parvoviridae that has been widely used as a vector for gene therapy… 
Highly Cited
2012
Highly Cited
2012
Differential integrity of TALE nuclease genes following adenoviral and lentiviral vector gene transfer into human cells
The array of genome editing strategies based on targeted double-stranded DNA break formation have recently been enriched through… 
Highly Cited
2010
Highly Cited
2010
Functional genomics, proteomics, and regulatory DNA analysis in isogenic settings using zinc finger nuclease-driven transgenesis into a safe harbor locus in the human genome.
Isogenic settings are routine in model organisms, yet remain elusive for genetic experiments on human cells. We describe the use… 
Highly Cited
2006
Highly Cited
2006
In contrast to AAV-mediated Cntf expression, AAV-mediated Gdnf expression enhances gene replacement therapy in rodent models of retinal degeneration.
Highly Cited
2000
Highly Cited
2000
Mutational Analysis of the Adeno-Associated Virus Type 2 (AAV2) Capsid Gene and Construction of AAV2 Vectors with Altered Tropism
ABSTRACT Adeno-associated virus type 2 (AAV2) has proven to be a valuable vector for gene therapy. Characterization of the… 
Highly Cited
1983
Highly Cited
1983
Rescue of adeno-associated virus from recombinant plasmids: Gene correction within the terminal repeats of AAV
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