alipogene tiparvovec

 
National Institutes of Health

Topic mentions per year

Topic mentions per year

2012-2018
02420122018

Papers overview

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2018
2018
One-year results are reported of the first lipoprotein lipase deficiency (LPLD) patient treated with alipogene tiparvovec, which… (More)
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Review
2017
Review
2017
A good understanding of the natural history of rare genetic lipid disorders is a pre-requisite for successful patient management… (More)
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Review
2016
Review
2016
Alipogene tiparvovec (Glybera) is a gene therapy product approved in Europe under the "exceptional circumstances" pathway as a… (More)
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2014
2014
Cellular immune responses to adeno-associated viral (AAV) vectors used for gene therapy have been linked to attenuated transgene… (More)
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Review
2014
Review
2014
Alipogene tiparvovec (Glybera(®)) is an adeno-associated virus serotype 1 (AAV1)-based gene therapy that has been developed for… (More)
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Highly Cited
2013
Highly Cited
2013
We describe the 2-year follow-up of an open-label trial (CT-AMT-011–01) of AAV1-LPLS447X gene therapy for lipoprotein lipase (LPL… (More)
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2013
2013
Homozygous lipoprotein lipase (LPL) deficiency is an ultra-orphan disease associated with increased rates of pancreatitis… (More)
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2013
2013
Alipogene tiparvovec is the first adeno-associated virus (AAV)-mediated gene therapy to be approved for the treatment of a… (More)
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2012
2012
A recent news article discussed the progress in gene therapy, a field that has had a number of major setbacks (Gene therapies… (More)
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2012
2012
The European Medicines Agency has recommended that alipogene tiparvovec (marketed as Glybera) be authorised for sale in the… (More)
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