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Replagal

National Institutes of Health

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agalsidase alfa

Papers overview

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2015
2015
Adult Fabry patients in Sweden - Baseline data and Outcome of Four-Year Enzyme Replacement Treatment in a Male Cohort without Proteinuria
Background: Fabry disease is a rare X-linked lysosomal storage disease caused by defective activity of the lysosomal enzyme… 
Review
2014
Review
2014
Agalsidase alfa for the treatment of fabry disease: a closer look
Enzyme replacement therapies substitute particular enzymes in individuals who have deficient or absent levels of enzymatic… 
2013
2013
Enzyme replacement therapy in two Japanese siblings with Fabry disease, and its effectiveness on angiokeratoma and neuropathic pain.
2012
2012
Agalsidasa alfa (Replagal®) i agalsidasa beta (Fabrazyme®) per al tractament de pacients amb malaltia de Fabry
Agalsidasa; Malaltia de Fabry; Revisio sistematica; Agalsidase; Fabry's disease; Clinical trial; Enfermedad de Fabry; Revision… 
2012
2012
Myozyme, Replagal, Fabrazyme en de strafrechtspraak
2010
2010
Shire's replacement enzymes validate gene activation
2007
2007
Agalsidase alfa (Replagal™) in the treatment of Anderson-Fabry disease
  • G. Pastores
  • Biologics : targets & therapy
  • 2007
  • Corpus ID: 17351645
Anderson-Fabry disease (AFD) is an X-linked storage disorder caused by a deficiency of the lysosomal hydrolase a-galactosidase A… 
2007
2007
Enzyme Replacement in Fabry Disease: The Essence Is in the Kidney
Fabry disease is an X-linked, single-gene defect caused by a deficiency of lysosomal -galactosidase A resulting in failure to… 
2003
2003
Comparative evaluation of α-galactosidase A infusions for treatment of Fabry disease
Enzyme therapy has proven safe and effective in preventing and reversing many manifestations in patients with Gaucher disease. On… 
2003
2003
Head‐impulse testing in Fabry disease ‐ vestibular function in male and female patients
Aim: To study the prevalence of peripheral vestibular deficit in male and female patients with Fabry disease and to assess the… 
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