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Transthyretin Antisense Oligonucleotide ISIS-TTR Rx
Known as:
ISIS-TTR Rx
, ISIS-TTRRx
, TTR ASO ISIS-TTR Rx
An antisense oligonucleotide (ASO) targeting transthyretin (TTR), which has potential use in the treatment of TTR amyloidosis (ATTR). Upon…
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National Institutes of Health
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Papers overview
Semantic Scholar uses AI to extract papers important to this topic.
2015
2015
Development of ISIS-TTR Rx for Transthyretin Familial Amyloid Polyneuropathy (TTR-FAP) (S34.009)
Frederick J. Derosier
,
Jesse Kwon
,
+4 authors
B. Monia
Neurology
2015
Corpus ID: 74722028
Objective: To treat Transthyretin Familial Amyloid Polyneuropathy (TTR-FAP) patients via reduction of mutated and wild-type TTR…
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2014
2014
Results of a Phase 2 Open-Label Study of ISIS-SMNRx in Patients with Infantile (Type 1) Spinal Muscular Atrophy (S6.003)
R. Finkel
,
J. Day
,
+13 authors
K. Bishop
Neurology
2014
Corpus ID: 70353539
Objective: This study was conducted to evaluate the safety, tolerability, pharmacokinetics, and clinical efficacy of multiple…
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2014
2014
G.O.18 Results of a phase 2 study of ISIS-SMNRx in children with spinal muscular atrophy
B. Darras
,
C. Chiriboga
,
+16 authors
K. Bishop
Neuromuscular Disorders
2014
Corpus ID: 54389396
2014
2014
G.O.17 Results of a phase 2 open-label study of ISIS-SMNRx in patients with infantile (Type 1) spinal muscular atrophy
R. Finkel
,
J. Day
,
+14 authors
K. Bishop
Neuromuscular Disorders
2014
Corpus ID: 54281059
Review
2013
Review
2013
A 180 MEV INJECTION UPGRADE DESIGN FOR THE ISIS SYNCHROTRON
J. Thomason
,
D. Findlay
,
+16 authors
M. Hughes
2013
Corpus ID: 76651567
ISIS is the spallation neutron source at the Rutherford Appleton Laboratory in the UK. Obsolescence and reliability issues are…
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2012
2012
6 Biomechanical Analysis of Restored Teeth with Cast Intra-Radicular Retainer with and Without Ferrule Isis Andréa
Venturini Pola Poiate
,
Edgard Poiate Junior
,
E. Ballester
2012
Corpus ID: 12484687
The intra-radicular post is used to provide retention to a core, but would also have the function of distributing the functional…
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2008
2008
The Effects of Sponge Haliclona sp and Gorgonian Isis hippuris Combination Extract on Histopathological Feature of Swiss Mice Liver
W. Widagdo
2008
Corpus ID: 54573819
Backgrounds: Sponge Haliclona sp and Gorgonian Isis hippuris are marine organisms whose extracts are potential for anticancer…
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2007
2007
Spectral Coherence Interferometry (SCI) for fast and rugged industrial applications
A. Knuttel
,
F. Rammrath
European Conference on Lasers and Electro-Optics…
2007
Corpus ID: 20607326
Summary form only given. Standard optical coherence tomography (OCT) has been proven to provide surface and general 3D metrology…
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1996
1996
Isis prerromana, Isis romana
Jaime Alvar
1996
Corpus ID: 164660708
1972
1972
JULIAN-HELIOS SARAPIS UND HELENA-ISIS. MIT 31 ABBILDUNGEN
L. Budde
1972
Corpus ID: 191903155
A HANAREB, A ENVIRON 70 KM DE L'ANTIQUE SUFETULA, LA TUNISIENNE SBEITLA, A ETE TROUVEE UNE LAMPE DE TERRE CUITE D'EPOQUE ROMAINE…
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