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ELOSULFASE ALFA

 
National Institutes of Health

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Related topics

7 relations
5 ML ELOSULFASE ALFA 1 MG/ML Injection5 ML ELOSULFASE ALFA 1 MG/ML Injection [Vimizim]Alpha-glucosidaseN-acetylgalactosamine-6-sulfatase
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Broader (1)

GALNS protein, human

Papers overview

Semantic Scholar uses AI to extract papers important to this topic.
2019
2019
Enzyme-Loaded Gel Core Nanostructured Lipid Carriers to Improve Treatment of Lysosomal Storage Diseases: Formulation and In Vitro Cellular Studies of Elosulfase Alfa-Loaded Systems
Mucopolysaccharidosis IVA (Morquio A) is a rare inherited metabolic disease caused by deficiency of the lysosomal enzyme N… Expand
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2017
2017
Long-term Immunogenicity of Elosulfase Alfa in the Treatment of Morquio A Syndrome: Results From MOR-005, a Phase III Extension Study.
PURPOSE Elosulfase alfa is an enzyme replacement therapy for the treatment of Morquio A syndrome (mucopolysaccharidosis IVA), a… Expand
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2017
2017
Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa
BackgroundThis post hoc subanalysis examined outcomes in adult patients with Morquio A (mucopolysaccharidosis IVA) who received… Expand
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2016
2016
Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome.
Long-term efficacy and safety of elosulfase alfa enzyme replacement therapy were evaluated in Morquio A patients over 96weeks… Expand
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Review
2016
Review
2016
Role of elosulfase alfa in mucopolysaccharidosis IVA
Mucopolysaccharidosis type IVA (MPS IVA or Morquio A) is an autosomal recessive lysosomal storage disease which results in a… Expand
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Review
2016
Review
2016
Elosulfase alfa (BMN 110) for the treatment of mucopolysaccharidosis IVA (Morquio A Syndrome)
  • C. Hendriksz
  • Expert review of clinical pharmacology
  • 2016
    • Corpus ID: 4113175
ABSTRACT Introduction: Morquio A syndrome is a rare, autosomal recessive, lysosomal storage disorder caused by a deficiency in… Expand
2015
2015
Enzyme Replacement Therapies and Immunogenicity in Lysosomal Storage Diseases: Is There a Pattern?
  • P. Harmatz
  • Clinical therapeutics
  • 2015
    • Corpus ID: 33758501
Lysosomal storage diseases arise because of genetic mutations that result in nonfunctioning or dysfunctional lysosomal enzymes… Expand
Review
2014
Review
2014
Elosulfase alfa.
Mucopolysaccharidosis type IVA (MPS IVA), also known as Morquio A syndrome, is an inherited, lysosomal storage disorder caused by… Expand
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