Treatment of carnitine deficiency

@article{Winter2004TreatmentOC,
  title={Treatment of carnitine deficiency},
  author={Susan C. Winter},
  journal={Journal of Inherited Metabolic Disease},
  year={2004},
  volume={26},
  pages={171-180}
}
  • S. Winter
  • Published 1 March 2003
  • Medicine, Biology
  • Journal of Inherited Metabolic Disease
Summary: Carnitine deficiency is a secondary complication of many inborn errors of metabolism. Pharmacological treatment with carnitine not only corrects the deficiency, it facilitates removal of accumulating toxic acyl intermediates and the generation of mitochondrial free coenzyme A (CoA). The United States Food and Drug Administration (US FDA) approved the use of carnitine for the treatment of inborn errors of metabolism in 1992. This approval was based on retrospective chart analysis of 90… 
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TLDR
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TLDR
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TLDR
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