Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool

@inproceedings{Ramsey2017RevisedHS,
  title={Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool},
  author={Danielle Ramsey and Mariacristina Scoto and Anna G Mayhew and Marion Main and Elena Stacy Mazzone and Jacqueline Montes and Roberto de Sanctis and Sally Dunaway Young and Rachel Salazar and Allan M. Glanzman and Amy E Pasternak and Janet Quigley and Elizabeth Mirek and Tina Duong and Richard Gee and Matthew Civitello and Gihan I. Tennekoon and Marika Pane and Maria Carmela Pera and Katharine M. D. Bushby and John W. Day and Basil T. Darras and Darryl C. De Vivo and Richard S. Finkel and Eugenio Mercuri and Francesco Muntoni},
  booktitle={PloS one},
  year={2017}
}
Recent translational research developments in Spinal Muscular Atrophy (SMA), outcome measure design and demands from regulatory authorities require that clinical outcome assessments are 'fit for purpose'. An international collaboration (SMA REACH UK, Italian SMA Network and PNCRN USA) undertook an iterative process to address discontinuity in the recorded performance of the Hammersmith Functional Motor Scale Expanded and developed a revised functional scale using Rasch analysis, traditional… CONTINUE READING
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