New therapies for muscular dystrophy: cautious optimism.

  title={New therapies for muscular dystrophy: cautious optimism.},
  author={Giulio Cossu and Maurilio Sampaolesi},
  journal={Trends in molecular medicine},
  volume={10 10},
The quest for a therapy for muscular dystrophy has been the driving force behind the past 40 years of advances in this field. Numerous results, such as the identification of satellite cells and gene mutations that are responsible for most forms of dystrophies, advances in gene transfer and modification technology and, more recently, stem cells, have fueled hopes. However, administering corticosteroids still remains the only effective treatment available. Several recent advances have uncovered a… CONTINUE READING

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