Networking for rare diseases: a necessity for Europe

  title={Networking for rare diseases: a necessity for Europe},
  author={S. Aym{\'e} and J. Schmidtke},
  journal={Bundesgesundheitsblatt - Gesundheitsforschung - Gesundheitsschutz},
  • S. Aymé, J. Schmidtke
  • Published 2007
  • Medicine
  • Bundesgesundheitsblatt - Gesundheitsforschung - Gesundheitsschutz
  • Most rare diseases are life-threatening and chronically debilitating conditions, and the vast majority of them are genetically determined. Their individually low prevalence requires special combined efforts to address them so as to improve diagnosis, care and prevention. Though it is difficult to develop a public health policy specific to each rare disease, it is possible to have a global rather than a piecemeal approach in the areas of scientific and biomedical research, drug research and… CONTINUE READING
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