Nature and Prevalence of Pain in Fabry Disease and Its Response to Enzyme Replacement Therapy—A Retrospective Analysis From the Fabry Outcome Survey

@article{Hoffmann2007NatureAP,
  title={Nature and Prevalence of Pain in Fabry Disease and Its Response to Enzyme Replacement Therapy—A Retrospective Analysis From the Fabry Outcome Survey},
  author={B. Hoffmann and M. Beck and G. Sunder-Plassmann and W. Borsini and R. Ricci and A. Mehta},
  journal={The Clinical Journal of Pain},
  year={2007},
  volume={23},
  pages={535-542}
}
  • B. Hoffmann, M. Beck, +3 authors A. Mehta
  • Published 2007
  • Medicine
  • The Clinical Journal of Pain
  • BackgroundFabry disease is a multisystemic life-threatening lysosomal storage disorder caused by deficiency of α-galactosidase A. Symptoms of the disease may occur in different organs including kidney, heart, and the nervous system. ObjectivesTo evaluate the nature and prevalence of pain in a large cohort of patients with Fabry disease and to assess the effect of enzyme replacement therapy (ERT) with agalsidase alfa. MethodsRetrospective analysis of the data of 752 patients with Fabry disease… CONTINUE READING
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