Multiple exon skipping strategies to by-pass dystrophin mutations

  title={Multiple exon skipping strategies to by-pass dystrophin mutations},
  author={L. Pirra},
  journal={Yearbook of Neurology and Neurosurgery},
  • L. Pirra
  • Published 2012
  • Medicine
  • Yearbook of Neurology and Neurosurgery

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Multiple exon skipping strategies to by-pass dystrophin mutations
This work presents strategies to by-pass intra-exonic dystrophin mutations that clearly demonstrate the importance of tailoring exon skipping strategies to specific patient mutations. Expand