Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease

@article{Stok2020LentiviralHS,
  title={Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease},
  author={Merel Stok and Helen de Boer and Marshall W. Huston and Ed Jacobs and Onno Roovers and Trudi P. Visser and Holger Jahr and Dirk Jan Duncker and Elza D van Deel and Arnold J. J. Reuser and Niek P. van Til and Gerard Wagemaker},
  journal={Molecular Therapy. Methods \& Clinical Development},
  year={2020},
  volume={17},
  pages={1014 - 1025}
}

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