Gene therapy for hemophilia.


Hemophilia A and B are X-linked genetic disorders caused by deficiency of the coagulation factors VIII and IX, respectively. Because of the health hazards and costs of current product replacement therapy, much effort is devoted to the development of gene therapy for these disorders. Approaches to gene therapy for the hemophilias include: ex vivo gene… (More)


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@article{Hortelano2000GeneTF, title={Gene therapy for hemophilia.}, author={Gonzalo Hortelano and P. L. Y. C. Chang}, journal={Artificial cells, blood substitutes, and immobilization biotechnology}, year={2000}, volume={28 1}, pages={1-24} }