Gene therapy for cystic fibrosis


Recent studies have identified the underlying molecular defect in cystic fibrosis (CF). Reduced or absent cAMP-mediated chloride transport in epithelial-lined organs characterizes this disease. With the identification of the CF gene, gene therapy has become a potential novel form of treatment for this disease. This article reviews the rapid progress in CF… (More)
DOI: 10.1007/BF00710061


Cite this paper

@article{Alton1995GeneTF, title={Gene therapy for cystic fibrosis}, author={Eric W. F. W. Alton}, journal={Journal of Inherited Metabolic Disease}, year={1995}, volume={18}, pages={501-507} }