Gene therapy finds its niche

@article{Sheridan2011GeneTF,
  title={Gene therapy finds its niche},
  author={Cormac Sheridan},
  journal={Nature Biotechnology},
  year={2011},
  volume={29},
  pages={121-128}
}
  • C. Sheridan
  • Published 7 February 2011
  • Medicine
  • Nature Biotechnology
Gene therapy is finally poised to make a contribution to the treatment of debilitating, highly penetrant genetic diseases that have proved intractable to other regimens. 

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