Gene therapy field hit by fresh safety concern.


A virus that buoyed the gene therapy field when it led to dramatic benefits in babies born with a fatal neuromuscular condition is under scrutiny. The success of the virus—a “vector” for therapeutic DNA—raised hopes that a similar approach could treat other diseases. But an animal study now suggests that the high doses of virus needed may not always be as… (More)
DOI: 10.1126/science.359.6376.621


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