Gene therapy ethics and haemophilia: an inevitable therapeutic future?

@article{Dimichele2003GeneTE,
  title={Gene therapy ethics and haemophilia: an inevitable therapeutic future?},
  author={Donna Dimichele and Franklin G. Miller and Joseph J. Fins},
  journal={Haemophilia : the official journal of the World Federation of Hemophilia},
  year={2003},
  volume={9 2},
  pages={145-52}
}
Haemophilia was recognized early on as an ideal candidate for a gene transfer approach to therapy. In the past decade, gene transfer experimentation in the haemophilias has indeed played an integral role in furthering the science in the global field of gene therapy. However, these expectations have placed haemophilia gene transfer researchers under pressure to succeed in a scientific domain in which successes are infrequent and progress is necessarily slow. These same expectations have also… CONTINUE READING