Content validity and clinical meaningfulness of the HFMSE in spinal muscular atrophy

@inproceedings{Pera2017ContentVA,
  title={Content validity and clinical meaningfulness of the HFMSE in spinal muscular atrophy},
  author={Maria Carmela Pera and Giorgia Coratti and Nicola Forcina and Elena Stacy Mazzone and Mariacristina Scoto and Jacqueline Montes and Amy E Pasternak and Anna G Mayhew and Sonia Messina and Maria Sframeli and Marion Main and Robert Muni Lofra and Tina Duong and Danielle Ramsey and Sally L Dunaway and Rachel Salazar and Lavinia Fanelli and Matthew Civitello and Roberto de Sanctis and Laura Antonaci and Leonardo Lapenta and Simona Lucibello and Marika Pane and John W. Day and Basil T. Darras and Darryl C. De Vivo and Francesco Muntoni and Richard S. Finkel and Eugenio Mercuri},
  booktitle={BMC neurology},
  year={2017}
}
BACKGROUND Reports on the clinical meaningfulness of outcome measures in spinal muscular atrophy (SMA) are rare. In this two-part study, our aim was to explore patients' and caregivers' views on the clinical relevance of the Hammersmith Functional Motor Scale Expanded- (HFMSE). METHODS First, we used focus groups including SMA patients and caregivers to explore their views on the clinical relevance of the individual activities included in the HFMSE. Then we asked caregivers to comment on the… CONTINUE READING
Recent Discussions
This paper has been referenced on Twitter 4 times over the past 90 days. VIEW TWEETS