• Corpus ID: 45818798

Bone marrow transplantation for inherited diseases.

  title={Bone marrow transplantation for inherited diseases.},
  author={A S O'Marcaigh and Morton J. Cowan},
  journal={Current opinion in oncology},
  volume={9 2},
Allogeneic bone marrow transplantation has been used successfully for the treatment of a variety of inherited diseases. The goal of transplantation in this setting is to provide a sufficient degree of sustained marrow engraftment to allow longterm amelioration of the inherited disease phenotype. Many factors influence the likelihood of achieving this goal, including donor availability, conditioning regimen, marrow processing, and the nature and extent of progression of the disease. For many… 
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