Agalsidase beta treatment is associated with improved quality of life in patients with Fabry disease: Findings from the Fabry Registry

  title={Agalsidase beta treatment is associated with improved quality of life in patients with Fabry disease: Findings from the Fabry Registry},
  author={Torquil Watt and A Burlina and Chiara Cazzorla and Dorothee Sch{\"o}nfeld and Maryam Banikazemi and Robert J Hopkin and Ana M Martins and Katherine Sims and Dana Beitner-Johnson and Fanny O'brien and Ulla Feldt-Rasmussen},
  journal={Genetics in Medicine},
Disclosure: The Fabry Registry is sponsored by Genzyme Corporation. U.F.-R., K.S., R.J.H., M.B., A.M., and A.P.B. serve on the Genzyme-sponsored Fabry Registry Boards of Advisors. D.B.-J. and F.O.B. are full-time employees of Genzyme Corporation. T.W. has received unrestricted grants from Genzyme for other research projects.Purpose: To evaluate the effect of agalsidase beta on longitudinal health-related quality of life in patients with Fabry disease.Methods: The SF-36® Health Survey was used… CONTINUE READING

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