[Orphan drugs and metabolic disorders].


INTRODUCTION Over the past twenty years the legal and philosophical concept of orphan diseases has developed to include the diseases with an incidence in the general population of less than 1/5,000. Treatment of these conditions, which is very specific, requires drugs which will be used by a very small number of patients and are therefore not profitable… (More)


Cite this paper

@article{MartnezPardo2001OrphanDA, title={[Orphan drugs and metabolic disorders].}, author={M. Rosa Infante Mart{\'i}nez-Pardo}, journal={Revista de neurologia}, year={2001}, volume={33 3}, pages={220-5} }