Targeting CAG repeat RNAs reduces Huntington's disease phenotype independently of huntingtin levels.Laura Rué, Mónica Báñez-Coronel, +10 authors Eulàlia MartíThe Journal of clinical investigation2016Huntington's disease (HD) is a polyglutamine disorder caused by a CAG expansion in the Huntingtin (HTT) gene exon 1. This expansion encodes a mutant protein whose abnormal function is traditionally… (More)